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NCT06655155From ClinicalTrials.govRecruiting

A Study to Assess the Efficacy and Safety of Efgartigimod PH20 SC in Adults With Systemic Sclerosis

A Randomized, Double-Blinded, Placebo-Controlled, Phase 2, Parallel-Group Study to Evaluate the Efficacy, Safety, Tolerability, Pharmacodynamics, Pharmacokinetics, and Immunogenicity of Efgartigimod PH20 SC in Adult Participants With Systemic Sclerosis

  • Systemic Sclerosis (SSc)

At a glance

Phase
Phase 2
Study type
Interventional
Sponsor
argenx
Enrolment target
81
Started
11 November 2024
Main results due
February 2027
Study sites
79
Registry updated
24 September 2026

Can you take part?

  • Aged 18 years and over.
  • Open to any sex.
  • You need the condition being studied — healthy volunteers are not accepted.

These are the headline rules only. Every study has a longer list, and whether you are eligible is decided by the research team at the site — never by this page.

Read the full eligibility criteria
Inclusion Criteria:

* Is aged ≥18 years and the local legal age of consent for clinical studies
* Has diffuse or limited SSc diagnosis and fulfills the 2013 ACR/EULAR classification criteria
* Has a positive antinuclear antibodies (ANA) test result at the central laboratory with titer of at least 1:160
* Has a Health Assessment Questionnaire-Disability Index (HAQ-DI) score of at least 0.5 OR a Patient Global Assessment (PGA) score of at least 3
* Has a modified Rodnan Skin Score (mRSS) score between 15 and 35
* The participant is anti-RNA polymerase III autoantibody negative at central laboratory and had the first non-Raynaud's phenomenon manifestation less than 5 years before screening or the participant is anti-RNA polymerase III autoantibody positive at central laboratory and had the first non-Raynaud's phenomenon manifestation less than 2 years before screening
* Has uninvolved or mildly thickened skin area in at least 1 injection site

Exclusion Criteria:

* Isolated anticentromere antibodies (ACA) seropositivity at the central laboratory
* Significant Pulmonary Arterial Hypertension
* Severe digital vasculopathy within the past 3 months
* Skin thickening due to scleroderma mimics or localized scleroderma
* Scleroderma renal crisis within the past 6 months of participating to the study
* Another rheumatic autoimmune disease, except for secondary Sjögren's syndrome or fibromyalgia

What this study is about

In the sponsor’s own words, from the registry.

The main purpose of this study is to evaluate the effect and safety of efgartigimod PH20 SC compared to placebo in adults with systemic sclerosis. The study consists of a screening period, a treatment period of up to 48 weeks and a safety follow-up period. After the screening period, eligible participants will be randomized in a 2:1 ratio to receive either efgartigimod PH20 SC or placebo. The total study duration can be up to approximately 15 months.

More information can be found on: https://clinicaltrials.argenx.com/esscape

Study sites(79)

  • Arizona Arthritis and Rheumatology Associates

    Phoenix, Arizona, United States

    Recruiting

  • UCLA Ronald Reagan University of California Los Angeles Medical Center

    Los Angeles, California, United States

    Recruiting

  • IRIS Research and Development LLC

    Plantation, Florida, United States

    Recruiting

  • University of Illinois Health Outpatient Care Center

    Chicago, Illinois, United States

    Recruiting

  • DelRicht Research, LLC

    New Orleans, Louisiana, United States

    Recruiting

  • Johns Hopkins Asthma and Allergy Center

    Baltimore, Maryland, United States

    Recruiting

  • Thomas Jefferson University

    Columbia, Maryland, United States

    Recruiting

  • University of Michigan Hospital

    Ann Arbor, Michigan, United States

    Recruiting

  • Perelman Center for Advanced Medicine

    Philadelphia, Pennsylvania, United States

    Recruiting

  • Aprillus Asistencia e Investigacion

    Buenos Aires, Argentina

    Recruiting

  • Instituto de Investigación Clínica TyT

    Buenos Aires, Argentina

    Recruiting

  • Consultorios Médicos Dr. Doreski - Fundacion Respirar

    Buenos Aires, Argentina

    Recruiting

  • Hospital General de Agudos Dr. José María Ramos Mejia

    Buenos Aires, Argentina

    Recruiting

  • Sanatorio Allende S.A.

    Córdoba, Argentina

    Recruiting

  • Centro de Investigaciones Reumatológicas

    San Miguel de Tucumán, Argentina

    Recruiting

  • Clínica Mayo de U.M.C.B. S.R.L

    San Miguel de Tucumán, Argentina

    Recruiting

  • Centro de Investigaciones Médicas Tucumán

    San Miguel de Tucumán, Argentina

    Recruiting

  • UZ Gent

    Ghent, Belgium

    Recruiting

  • UZ Brussel

    Jette, Belgium

    Recruiting

  • Medical Center Artmed OOD

    Plovdiv, Bulgaria

    Recruiting

  • Diagnostic Consultative Center Convex EOOD

    Sofia, Bulgaria

    Recruiting

  • BIOCINETIC Ltda

    Santiago, Chile

    Recruiting

  • Centro de Investigaciones Clinicas UC (CICUC)

    Santiago, Chile

    Recruiting

  • Centro de especialidades médicas Vanguardia

    Temuco, Chile

    Recruiting

  • Clinical Hospital Centre Osijek

    Osijek, Croatia

    Recruiting

  • University Hospital of Split

    Split, Croatia

    Recruiting

  • General Hospital Zadar

    Zadar, Croatia

    Recruiting

  • Revmatologicky Ustav

    Prague, Czechia

    Recruiting

  • Rigshospitalet

    Copenhagen, Denmark

    Recruiting

  • CHU de Lille - Hopital Claude Huriez

    Lille, Nord, France

    Recruiting

  • CHU de Bordeaux - Hôpital Pellegrin

    Bordeaux, France

    Recruiting

  • CHU de Lille - Hopital Claude Huriez

    Lille, France

    Recruiting

  • CHU de Strasbourg - Hôpital de Hautepierre

    Marseille, France

    Recruiting

  • CHU de Montpellier- Hôpital Saint Eloi

    Montpellier, France

    Recruiting

  • AP-HP - Hôpital Cochin - Port-Royal, site Cochin

    Paris, France

    Recruiting

  • Auenlandklinik Bad Bramstedt GmbH

    Bad Bramstedt, Germany

    Recruiting

  • Universitätsklinikum Schleswig-Holstein - Campus Lübeck

    Lübeck, Germany

    Recruiting

  • Mühlenkreiskliniken - Johannes Wesling Klinikum Minden

    Minden, Germany

    Recruiting

  • Universitätsklinikum Tübingen

    Tübingen, Germany

    Recruiting

  • Olympion General Clinic

    Pátrai, Greece

    Recruiting

  • University General Hospital of Patras

    Pátrai, Greece

    Recruiting

  • Euromedica Kianous Stavros

    Thessaloniki, Greece

    Recruiting

  • Pecsi Tudomanyegyetem, Klinika Kozpont, Bor, Nemikortani es Onkodermatologiai Klinika

    Pécs, Hungary

    Recruiting

  • Azienda Ospedaliera Universitaria Careggi

    Florence, Italy

    Recruiting

  • Ospedale San Raffaele S.r.l.

    Milan, Italy

    Recruiting

  • Azienda Ospedaliero-Universitaria di Modena - Policlinico di Modena

    Modena, Italy

    Recruiting

  • Azienda Ospedaliera Universitaria Luigi Vanvitelli

    Naples, Italy

    Recruiting

  • Fondazione Policlinico Universitario A. Gemelli IRCCS

    Roma, Italy

    Recruiting

  • Fondazione Policlinico Universitario Campus Bio-Medico

    Roma, Italy

    Recruiting

  • IRCCS Istituto Clinico Humanitas

    Rozzano, Italy

    Recruiting

  • Hospital of Lithuanian University of Health Sciences Kauno klinikos

    Kaunas, Lithuania

    Recruiting

  • Klaipeda Hospital, Affiliate of Klaipeda University Hospital

    Klaipėda, Lithuania

    Recruiting

  • Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran

    Belisario Domínguez, Tlalpan, Mexico

    Recruiting

  • Mediadvance Clinical S.A.P.I. de C.V.

    Chihuahua City, Mexico

    Recruiting

  • Centro Integral Reumatologia SA de CV

    Guadalajara, Mexico

    Recruiting

  • Centro de Investigación y Tratamiento Reumatológico S.C

    Mexico City, Mexico

    Recruiting

  • Medical Care and Research S.A. de C.V.

    Mérida, Mexico

    Recruiting

  • Leids Universitair Medisch Centrum

    Leiden, Netherlands

    Recruiting

  • Malopolskie Badania Kliniczne

    Krakow, Poland

    Recruiting

  • Zespol Poradni Specjalistycznych REUMED

    Lublin, Poland

    Recruiting

Showing 60 of 79 sites — filter to narrow it down. 79 of the 79 sites on this study are recruiting right now — a site can stop enrolling while the study as a whole is still open.

Source: ClinicalTrials.gov record NCT06655155. Trialion does not run this study, is not paid to refer anyone to it, and cannot enrol you. Eligibility is always decided by the research team at the site.

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A Study to Assess the Efficacy and Safety of Efgartigimod PH20 SC in Adults With Systemic Sclerosis | Trialion